Table of Content 1 Introduction 1.1 Objective of the Study 1.2 Definition of the Market 1.3 Market Scope 1.3.1 Market Segment by Type, Application and Marketing Channel 1.3.2 Major Regions Covered (North America, Europe, Asia Pacific, Mid East & Africa) 1.4 Years Considered for the Study (2014-2026) 1.5 Currency Considered (U.S. Dollar) 1.6 Stakeholders 2 Key Findings of the Study 3 Market Dynamics 3.1 Driving Factors for this Market 3.2 Factors Challenging the Market 3.3 Opportunities of the Global Batten Disease Market (Regions, Growing/Emerging Downstream Market Analysis) 3.4 Technological and Market Developments in the Batten Disease Market 3.5 Industry News by Region 3.6 Regulatory Scenario by Region/Country 3.7 Market Investment Scenario Strategic Recommendations Analysis 4 Value Chain of the Batten Disease Market 4.1 Value Chain Status 4.2 Upstream Raw Material Analysis 4.3 Midstream Major Company Analysis (by Manufacturing Base, by Product Type) 4.4 Distributors/Traders 4.5 Downstream Major Customer Analysis (by Region) 5 Global Batten Disease Market-Segmentation by Type 5.1 Occupational Therapies 5.2 Physical Therapies 6 Global Batten Disease Market-Segmentation by Application 6.1 Infantile NCL 6.2 Late Infantile NCL 6.3 Juvenile NCL 6.4 Adult NCL 7 Global Batten Disease Market-Segmentation by Marketing Channel 7.1 Traditional Marketing Channel (Offline) 7.2 Online Channel 8 Competitive Intelligence – Company Profiles 8.1 Ionis Pharmaceuticals 8.1.1 Ionis Pharmaceuticals Profile 8.1.2 Ionis Pharmaceuticals Sales, Growth Rate and Global Market Share from 2014-2019E 8.1.3 Ionis Pharmaceuticals Product/Solution Launches and Enhancements Analysis 8.1.4 Ionis Pharmaceuticals Business Overview/Recent Development/Acquisitions 8.2 RegenxBio 8.2.1 RegenxBio Profile 8.2.2 RegenxBio Sales, Growth Rate and Global Market Share from 2014-2019E 8.2.3 RegenxBio Product/Solution Launches and Enhancements Analysis 8.2.4 RegenxBio Business Overview/Recent Development/Acquisitions 8.3 Mitochon Pharmaceuticals 8.3.1 Mitochon Pharmaceuticals Profile 8.3.2 Mitochon Pharmaceuticals Sales, Growth Rate and Global Market Share from 2014-2019E 8.3.3 Mitochon Pharmaceuticals Product/Solution Launches and Enhancements Analysis 8.3.4 Mitochon Pharmaceuticals Business Overview/Recent Development/Acquisitions 8.4 BioMarin Pharmaceuticals 8.4.1 BioMarin Pharmaceuticals Profile 8.4.2 BioMarin Pharmaceuticals Sales, Growth Rate and Global Market Share from 2014-2019E 8.4.3 BioMarin Pharmaceuticals Product/Solution Launches and Enhancements Analysis 8.4.4 BioMarin Pharmaceuticals Business Overview/Recent Development/Acquisitions 8.5 Abeo Therapeutics 8.5.1 Abeo Therapeutics Profile 8.5.2 Abeo Therapeutics Sales, Growth Rate and Global Market Share from 2014-2019E 8.5.3 Abeo Therapeutics Product/Solution Launches and Enhancements Analysis 8.5.4 Abeo Therapeutics Business Overview/Recent Development/Acquisitions 8.6 CereSpir Inc 8.6.1 CereSpir Inc Profile 8.6.2 CereSpir Inc Sales, Growth Rate and Global Market Share from 2014-2019E 8.6.3 CereSpir Inc Product/Solution Launches and Enhancements Analysis 8.6.4 CereSpir Inc Business Overview/Recent Development/Acquisitions 8.7 Polaryx Therapeutics 8.7.1 Polaryx Therapeutics Profile 8.7.2 Polaryx Therapeutics Sales, Growth Rate and Global Market Share from 2014-2019E 8.7.3 Polaryx Therapeutics Product/Solution Launches and Enhancements Analysis 8.7.4 Polaryx Therapeutics Business Overview/Recent Development/Acquisitions 8.8 Seneb BioSciences. 8.8.1 Seneb BioSciences. Profile 8.8.2 Seneb BioSciences. Sales, Growth Rate and Global Market Share from 2014-2019E 8.8.3 Seneb BioSciences. Product/Solution Launches and Enhancements Analysis 8.8.4 Seneb BioSciences. Business Overview/Recent Development/Acquisitions 8.9 Evotec AG 8.9.1 Evotec AG Profile 8.9.2 Evotec AG Sales, Growth Rate and Global Market Share from 2014-2019E 8.9.3 Evotec AG Product/Solution Launches and Enhancements Analysis 8.9.4 Evotec AG Business Overview/Recent Development/Acquisitions 8.10 Spark Therapeutics 8.10.1 Spark Therapeutics Profile 8.10.2 Spark Therapeutics Sales, Growth Rate and Global Market Share from 2014-2019E 8.10.3 Spark Therapeutics Product/Solution Launches and Enhancements Analysis 8.10.4 Spark Therapeutics Business Overview/Recent Development/Acquisitions 9 Global Batten Disease Market-Segmentation by Geography 10 North America 10.1 North America Batten Disease Production, Ex-factory Price, Revenue, Gross Margin (%) and Gross Analysis from 2014-2019E 10.2 North America Batten Disease Consumption, Terminal Price, Consumption Value and Channel Margin Analysis from 2014-2019E 10.3 North America Batten Disease Production Analysis from 2014-2019E 10.4 North America Batten Disease Consumption Analysis from 2014-2019E 10.5 North America Batten Disease Import and Export from 2014-2019E 10.6 North America Batten Disease Value, Production and Market Share by Type (2014-2019E) 10.7 North America Batten Disease Consumption, Value and Market Share by Application (2014-2019E) 10.8 North America Batten Disease by Country (United States, Canada) 10.8.1 North America Batten Disease Sales by Country (2014-2019E) 10.8.2 North America Batten Disease Consumption Value by Country (2014-2019E) 10.9 North America Batten Disease Market PEST Analysis 11 Europe 11.1 Europe Batten Disease Production, Ex-factory Price, Revenue, Gross Margin (%) and Gross Analysis from 2014-2019E 11.2 Europe Batten Disease Consumption, Terminal Price, Consumption Value and Channel Margin Analysis from 2014-2019E 11.3 Europe Batten Disease Production Analysis from 2014-2019E 11.4 Europe Batten Disease Consumption Analysis from 2014-2019E 11.5 Europe Batten Disease Import and Export from 2014-2019E 11.6 Europe Batten Disease Value, Production and Market Share by Type (2014-2019E) 11.7 Europe Batten Disease Consumption, Value and Market Share by Application (2014-2019E) 11.8 Europe Batten Disease by Country (Germany, UK, France, Italy, Spain, Russia, Netherlands, Turkey, Switzerland, Sweden, Poland, Belgium) 11.8.1 Europe Batten Disease Sales by Country (2014-2019E) 11.8.2 Europe Batten Disease Consumption Value by Country (2014-2019E) 11.9 Europe Batten Disease Market PEST Analysis 12 Asia-Pacific 12.1 Asia-Pacific Batten Disease Production, Ex-factory Price, Revenue, Gross Margin (%) and Gross Analysis from 2014-2019E 12.2 Asia-Pacific Batten Disease Consumption, Terminal Price, Consumption Value and Channel Margin Analysis from 2014-2019E 12.3 Asia-Pacific Batten Disease Production Analysis from 2014-2019E 12.4 Asia-Pacific Batten Disease Consumption Analysis from 2014-2019E 12.5 Asia-Pacific Batten Disease Import and Export from 2014-2019E 12.6 Asia-Pacific Batten Disease Value, Production and Market Share by Type (2014-2019E) 12.7 Asia-Pacific Batten Disease Consumption, Value and Market Share by Application (2014-2019E) 12.8 Asia-Pacific Batten Disease by Country (China, Japan, South Korea, Australia, India, Taiwan, Indonesia, Thailand, Philippines, Malaysia) 12.8.1 Asia-Pacific Batten Disease Sales by Country (2014-2019E) 12.8.2 Asia-Pacific Batten Disease Consumption Value by Country (2014-2019E) 12.9 Asia-Pacific Batten Disease Market PEST Analysis 13 Latin America 13.1 Latin America Batten Disease Production, Ex-factory Price, Revenue, Gross Margin (%) and Gross Analysis from 2014-2019E 13.2 Latin America Batten Disease Consumption, Terminal Price, Consumption Value and Channel Margin Analysis from 2014-2019E 13.3 Latin America Batten Disease Production Analysis from 2014-2019E 13.4 Latin America Batten Disease Consumption Analysis from 2014-2019E 13.5 Latin America Batten Disease Import and Export from 2014-2019E 13.6 Latin America Batten Disease Value, Production and Market Share by Type (2014-2019E) 13.7 Latin America Batten Disease Consumption, Value and Market Share by Application (2014-2019E) 13.8 Latin America Batten Disease by Country (Brazil, Mexico, Argentina, Columbia, Chile) 13.8.1 Latin America Batten Disease Sales by Country (2014-2019E) 13.8.2 Latin America Batten Disease Consumption Value by Country (2014-2019E) 13.9 Latin America Batten Disease Market PEST Analysis 14 Middle East & Africa 14.1 Middle East & Africa Batten Disease Production, Ex-factory Price, Revenue, Gross Margin (%) and Gross Analysis from 2014-2019E 14.2 Middle East & Africa Batten Disease Consumption, Terminal Price, Consumption Value and Channel Margin Analysis from 2014-2019E 14.3 Middle East & Africa Batten Disease Production Analysis from 2014-2019E 14.4 Middle East & Africa Batten Disease Consumption Analysis from 2014-2019E 14.5 Middle East & Africa Batten Disease Import and Export from 2014-2019E 14.6 Middle East & Africa Batten Disease Value, Production and Market Share by Type (2014-2019E) 14.7 Middle East & Africa Batten Disease Consumption, Value and Market Share by Application (2014-2019E) 14.8 Middle East & Africa Batten Disease by Country (Saudi Arabia, UAE, Egypt, Nigeria, South Africa) 14.8.1 Middle East & Africa Batten Disease Sales by Country (2014-2019E) 14.8.2 Middle East & Africa Batten Disease Consumption Value by Country (2014-2019E) 14.9 Middle East & Africa Batten Disease Market PEST Analysis 15 Future Forecast of the Global Batten Disease Market from 2018-2026 15.1 Future Forecast of the Global Batten Disease Market from 2019-2026 Segment by Region 15.2 Global Batten Disease Production and Growth Rate Forecast by Type (2019-2026) 15.3 Global Batten Disease Consumption and Growth Rate Forecast by Application (2019-2026) 16 Appendix 16.1 Methodology 16.2 Research Data Source

List of Tables and Figures Global Batten Disease Market Value ($) and Growth Rate of Batten Disease from 2014-2026 Global Batten Disease Production and Growth Rate Segment by Product Type from 2014-2026F Global Batten Disease Consumption and Growth Rate Segment by Application from 2014-2019E Figure Batten Disease Picture Table Product Specifications of Batten Disease Table Driving Factors for this Market Table Industry News of Batten Disease Market Figure Value Chain Status of Batten Disease Table Midstream Major Company Analysis (by Manufacturing Base, by Product Type) Table Distributors/Traders Table Downstream Major Customer Analysis (by Region, by Preference) Table Global Batten Disease Production and Growth Rate Segment by Product Type from 2014-2019E Table Global Batten Disease Value ($) and Growth Rate Segment by Product Type from 2014-2019E Figure Occupational Therapies of Batten Disease Figure Physical Therapies of Batten Disease Table Global Batten Disease Consumption and Growth Rate Segment by Application from 2014-2019E Table Global Batten Disease Value ($) and Growth Rate Segment by Application from 2014-2019E Figure Infantile NCL of Batten Disease Figure Late Infantile NCL of Batten Disease Figure Juvenile NCL of Batten Disease Figure Adult NCL of Batten Disease Table Global Batten Disease Consumption and Growth Rate Segment by Marketing Channel from 2014-2019E Table Global Batten Disease Value ($) and Growth Rate Segment by Marketing Channel from 2014-2019E Figure Traditional Marketing Channel (Offline) of Batten Disease Figure Online Channel of Batten Disease Table Ionis Pharmaceuticals Profile (Company Name, Plants Distribution, Sales Region) Figure Ionis Pharmaceuticals Sales and Growth Rate from 2014-2019E Figure Ionis Pharmaceuticals Revenue ($) and Global Market Share from 2014-2019E Table Ionis Pharmaceuticals Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table RegenxBio Profile (Company Name, Plants Distribution, Sales Region) Figure RegenxBio Sales and Growth Rate from 2014-2019E Figure RegenxBio Revenue ($) and Global Market Share from 2014-2019E Table RegenxBio Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Mitochon Pharmaceuticals Profile (Company Name, Plants Distribution, Sales Region) Figure Mitochon Pharmaceuticals Sales and Growth Rate from 2014-2019E Figure Mitochon Pharmaceuticals Revenue ($) and Global Market Share from 2014-2019E Table Mitochon Pharmaceuticals Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table BioMarin Pharmaceuticals Profile (Company Name, Plants Distribution, Sales Region) Figure BioMarin Pharmaceuticals Sales and Growth Rate from 2014-2019E Figure BioMarin Pharmaceuticals Revenue ($) and Global Market Share from 2014-2019E Table BioMarin Pharmaceuticals Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Abeo Therapeutics Profile (Company Name, Plants Distribution, Sales Region) Figure Abeo Therapeutics Sales and Growth Rate from 2014-2019E Figure Abeo Therapeutics Revenue ($) and Global Market Share from 2014-2019E Table Abeo Therapeutics Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table CereSpir Inc Profile (Company Name, Plants Distribution, Sales Region) Figure CereSpir Inc Sales and Growth Rate from 2014-2019E Figure CereSpir Inc Revenue ($) and Global Market Share from 2014-2019E Table CereSpir Inc Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Polaryx Therapeutics Profile (Company Name, Plants Distribution, Sales Region) Figure Polaryx Therapeutics Sales and Growth Rate from 2014-2019E Figure Polaryx Therapeutics Revenue ($) and Global Market Share from 2014-2019E Table Polaryx Therapeutics Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Seneb BioSciences. Profile (Company Name, Plants Distribution, Sales Region) Figure Seneb BioSciences. Sales and Growth Rate from 2014-2019E Figure Seneb BioSciences. Revenue ($) and Global Market Share from 2014-2019E Table Seneb BioSciences. Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Evotec AG Profile (Company Name, Plants Distribution, Sales Region) Figure Evotec AG Sales and Growth Rate from 2014-2019E Figure Evotec AG Revenue ($) and Global Market Share from 2014-2019E Table Evotec AG Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Spark Therapeutics Profile (Company Name, Plants Distribution, Sales Region) Figure Spark Therapeutics Sales and Growth Rate from 2014-2019E Figure Spark Therapeutics Revenue ($) and Global Market Share from 2014-2019E Table Spark Therapeutics Batten Disease Sales, Price, Revenue, Gross Margin (2014-2019E) Table Global Batten Disease Production Value ($) by Region from 2014-2019E Table Global Batten Disease Production Value Share by Region from 2014-2019E Table Global Batten Disease Production by Region from 2014-2019E Table Global Batten Disease Consumption Value ($) by Region from 2014-2019E Table Global Batten Disease Consumption by Region from 2014-2019E Table North America Batten Disease Production, Ex-factory Price Revenue ($), Gross Margin (%) and Gross ($) Analysis from 2014-2019E Table North America Batten Disease Consumption, Terminal Price, Consumption Value ($) and Channel Margin Analysis from 2014-2019E Table North America Batten Disease Import and Export from 2014-2019E Table North America Batten Disease Value ($) by Type (2014-2019E) Table North America Batten Disease Production by Type (2014-2019E) Table North America Batten Disease Consumption by Application (2014-2019E) Table North America Batten Disease Consumption by Country (2014-2019E) Table North America Batten Disease Consumption Value ($) by Country (2014-2019E) Figure North America Batten Disease Market PEST Analysis Table Europe Batten Disease Production, Ex-factory Price Revenue ($), Gross Margin (%) and Gross ($) Analysis from 2014-2019E Table Europe Batten Disease Consumption, Terminal Price, Consumption Value ($) and Channel Margin Analysis from 2014-2019E Table Europe Batten Disease Import and Export from 2014-2019E Table Europe Batten Disease Value ($) by Type (2014-2019E) Table Europe Batten Disease Production by Type (2014-2019E) Table Europe Batten Disease Consumption by Application (2014-2019E) Table Europe Batten Disease Consumption by Country (2014-2019E) Table Europe Batten Disease Consumption Value ($) by Country (2014-2019E) Figure Europe Batten Disease Market PEST Analysis Table Asia-Pacific Batten Disease Production, Ex-factory Price Revenue ($), Gross Margin (%) and Gross ($) Analysis from 2014-2019E Table Asia-Pacific Batten Disease Consumption, Terminal Price, Consumption Value ($) and Channel Margin Analysis from 2014-2019E Table Asia-Pacific Batten Disease Import and Export from 2014-2019E Table Asia-Pacific Batten Disease Value ($) by Type (2014-2019E) Table Asia-Pacific Batten Disease Production by Type (2014-2019E) Table Asia-Pacific Batten Disease Consumption by Application (2014-2019E) Table Asia-Pacific Batten Disease Consumption by Country (2014-2019E) Table Asia-Pacific Batten Disease Consumption Value ($) by Country (2014-2019E) Figure Asia-Pacific Batten Disease Market PEST Analysis Table Latin America Batten Disease Production, Ex-factory Price Revenue ($), Gross Margin (%) and Gross ($) Analysis from 2014-2019E Table Latin America Batten Disease Consumption, Terminal Price, Consumption Value ($) and Channel Margin Analysis from 2014-2019E Table Latin America Batten Disease Import and Export from 2014-2019E Table Latin America Batten Disease Value ($) by Type (2014-2019E) Table Latin America Batten Disease Production by Type (2014-2019E) Table Latin America Batten Disease Consumption by Application (2014-2019E) Table Latin America Batten Disease Consumption by Country (2014-2019E) Table Latin America Batten Disease Consumption Value ($) by Country (2014-2019E) Figure Latin America Batten Disease Market PEST Analysis Table Middle East & Africa Batten Disease Production, Ex-factory Price Revenue ($), Gross Margin (%) and Gross ($) Analysis from 2014-2019E Table Middle East & Africa Batten Disease Consumption, Terminal Price, Consumption Value ($) and Channel Margin Analysis from 2014-2019E Table Middle East & Africa Batten Disease Import and Export from 2014-2019E Table Middle East & Africa Batten Disease Value ($) by Type (2014-2019E) Table Middle East & Africa Batten Disease Production by Type (2014-2019E) Table Middle East & Africa Batten Disease Consumption by Application (2014-2019E) Table Middle East & Africa Batten Disease Consumption by Country (2014-2019E) Table Middle East & Africa Batten Disease Consumption Value ($) by Country (2014-2019E) Figure Middle East & Africa Batten Disease Market PEST Analysis Table Global Batten Disease Value ($) and Growth Rate Forecast by Region (2018-2026) Table Global Batten Disease Production and Growth Rate Forecast by Region (2019-2026) Table Global Batten Disease Consumption and Growth Rate Forecast by Region (2019-2026) Table Global Batten Disease Production and Growth Rate Forecast by Type (2019-2026) Table Global Batten Disease Consumption and Growth Rate Forecast by Application (2019-2026)